Treatment Options for Patients with Sickle Cell Disease

Can a bone marrow transplant or gene therapy cure sickle cell disease? Get the facts.

Printer-friendly versionPDF version Register Now
Wednesday, August 11, 2021

Treatment Options for Patients with Sickle Cell Disease

Wednesday, August 11, 2021 

Time:   7:00 pm Eastern;  6:00 pm Central;  5:00 pm Mountain;  4:00 pm Pacific

Duration:  40 minute presentation followed by questions and answers.

Presenters: Hemalatha Rangarajan MD, Pediatric Stem Cell Transplant Physician, Nationwide Children's Hospital; and Alison Towerman, RN, MSN,  Pediatric Nurse Practitioner, St. Louis Children's Hospital at Washington University School of Medicine

What you will learn:

Sickle cell disease (SCD) is an inherited blood disorder that affects millions of people throughout the world. It is particularly common among those whose ancestors came from sub-Saharan African; Spanish-speaking regions in the Western Hemisphere (South America, the Caribbean and Central America); Saudi Arabia; India; and Mediterranean countries such as Turkey, Greece and Italy. Sickle cell disease affects and estimated 100,000 people living in the U.S.

People with sickle cell disease are at greater risk than the general population for stroke, bacterial infections, kidney failure and lung disease which can lead to premature death. Severe pain is also common among those living with sickle cell disease.

Learn about two promising treatment options for patients sickle cell disease -  a bone marrow transplant and gene therapy - in this free webinar from BMT InfoNet.


  • What are the steps involved in undergoing a bone marrow transplant?
  • What steps are involved in gene therapy?
  • What is the likely outcome after a bone marrow transplant or gene therapy?

Bring your questions!

The webinar is free, but advance registration is required.  All you will need to participate is a computer, smart phone or other electronic device.

About the Speakers

Dr. Hemalatha Rangarajan is a pediatric stem cell transplant physician who specializes in the care of children and young adults with sickle cell disease. Her research interests include optimizing transplantation strategies, supportive care measures, and exploring the use of non-sibling donors in patients with sickle cell disease. She is working with colleagues nationally on clinical trials to reduce the toxicity and complications of bone marrow transplant without compromising its effectiveness, and making them more available to SCD patients. Dr. Rangarajan is a member of the Scientific Executive Committee of the Sickle Cell Transplant and Advocacy and Research Alliance (STAR) consortium, a large non-profit organization focused on research to cure sickle cell disease.

Alison Towerman is a pediatric nurse practitioner at St. Louis Children’s Hospital/Washington University School of Medicine. She has been caring for children and adolescents with sickle cell disease for nearly nine years. She is interested in promoting disease-modifying therapy for improved quality of life, and providing children with sickle cell disease an opportunity for a cure. She helped establish a Survivorship Clinic at St. Louis Children’s Hospital for patients with sickle cell disease, who have undergone transplant, recognizing their unique long-term issues due to their disease. She is also a member of the STAR consortium.